Building healthier futures powered by thoughtful science

We are a highly focused, research-driven biopharmaceutical company working in rare diseases. We're exploring the potential of cutting-edge science as a subsidiary of Nippon Shinyaku Co., Ltd. In Japan.

Advancing rare disease research

Inspired by our own families, as well as the individuals we aim to provide with treatment, NS Pharma is conducting advanced research in rare diseases, including exon-skipping technology, to offer new, effective treatment options for Duchenne. We’re also developing JAK1 inhibition for the potential treatment of eosinophilic granulomatosis with polyangiitis (EGPA).

Therapeutic areas

NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.

Scientific approaches

Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.

Therapeutic areas

NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.

Scientific approaches

Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.

From our blog

Press Release / September 9, 2025

FDA Grants Fast Track Designation to NS-229 for the Treatment of Eosinophilic Granulomatosis with Polyangiitis

Press Release / July 1, 2025

NS Pharma Announces Strategic Alliance with Boston Children’s Hospital to Develop New Therapies for Rare Diseases

Press Release / May 14, 2025

FDA Accepts Biologics License Application for Mucopolysaccharidosis II Treatment

Press Release / September 9, 2025

FDA Grants Fast Track Designation to NS-229 for the Treatment of Eosinophilic Granulomatosis with Polyangiitis

Press Release / July 1, 2025

NS Pharma Announces Strategic Alliance with Boston Children’s Hospital to Develop New Therapies for Rare Diseases

Press Release / May 14, 2025

FDA Accepts Biologics License Application for Mucopolysaccharidosis II Treatment

Social media

We’re teeing off for the 18th Annual Team Joseph Golf Tournament today! ⛳

More than golf - today’s about raising vital funds for Duchenne research & family support.

Join NS Pharma in fueling progress: https://givebutter.com/tjgolftournament

#TeamJosephGolf #Duchenne #NSPharma #Community https://x.com/NSPharmaInc/status/1967589925592727839/photo/1

Join us in Philadelphia this September for the FREE #CureDuchenne Workshop! Where families, caregivers and experts unite for learning, support, and connection.

Save your spot: https://ow.ly/x1Vf50WQiAG

#DuchenneAwareness #CaregiverSupport #CommunityMatters https://x.com/NSPharmaInc/status/1966502372022067221/photo/1

This week, our brand ambassador Jordan picked his very first habaneros of the season which were perfect for making his famous JJ’s Firehouse Jam!🌶️🔥

His dedication reminds us how the right tools and a little creativity can make hobbies not just possible, but truly thriving. https://x.com/NSPharmaInc/status/1966167149107622229/photo/1

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A huge thank you to the @JettFoundation for hosting such an unforgettable weekend in Boston for #WorldDuchenneAwarenessDay!

Our team had an amazing time connecting, sharing stories, and celebrating the strength and spirit of the Duchenne community.

#WDAD #DMD #Duchenne https://x.com/NSPharmaInc/status/1965777283458662621/photo/1

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We’re excited to share that the FDA has granted Fast Track designation to NS-229 for Eosinophilic Granulomatosis with Polyangiitis (#EGPA), a rare autoimmune disease!

Read the full announcement: https://ow.ly/h95w50WTUFl

#RareDiseases #FDAFastTrack #PharmaInnovation https://x.com/NSPharmaInc/status/1965421247375765516/photo/1

Join our very own Lucy Luther at #FiercePharmaWeek 2025 in Philadelphia! 🌟

This is a unique opportunity to connect, share insights & collaborate on advancing therapies that make a difference for patients everywhere.

Learn more: https://ow.ly/Zs4l50WP6V1

#FPWRisingStars2025 https://x.com/NSPharmaInc/status/1965052837877977579/photo/1

Rocking our Duchenne Awareness Day tees today!👕✨

We're honored to be a sponsor of #WorldDuchenneAwarenessDay this weekend, brought to life by the @JettFoundation. Here's to making this year's louder than ever!

Learn more: https://www.jettfoundation.org/wdad/

#WDAD2025 #Duchenne https://x.com/NSPharmaInc/status/1963965348341752262/photo/1

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