Building healthier futures powered by thoughtful science
We are a highly focused, research-driven biopharmaceutical company working in rare diseases. We're exploring the potential of cutting-edge science as a subsidiary of Nippon Shinyaku Co., Ltd. In Japan.
Advancing rare disease research
Inspired by our own families, as well as the individuals we aim to provide with treatment, NS Pharma is conducting advanced research in rare diseases, including exon-skipping technology, to offer new, effective treatment options for Duchenne. We’re also developing JAK1 inhibition for the potential treatment of eosinophilic granulomatosis with polyangiitis (EGPA).
Therapeutic areas
NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.
Scientific approaches
Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.
Therapeutic areas
NS Pharma is working to have an important impact on the lives of patients with rare diseases. Our therapeutic areas encompass neurological diseases and inflammatory diseases.
Scientific approaches
Harnessing the power of innovative science can help bring new treatments to patients with rare diseases. NS Pharma is developing therapies through exon-skipping, cell therapy and JAK1 inhibition technology.
From our blog
Press Release / September 9, 2025
FDA Grants Fast Track Designation to NS-229 for the Treatment of Eosinophilic Granulomatosis with Polyangiitis
Press Release / July 1, 2025
NS Pharma Announces Strategic Alliance with Boston Children’s Hospital to Develop New Therapies for Rare Diseases
Press Release / May 14, 2025
FDA Accepts Biologics License Application for Mucopolysaccharidosis II Treatment
Press Release / September 9, 2025
FDA Grants Fast Track Designation to NS-229 for the Treatment of Eosinophilic Granulomatosis with Polyangiitis
Press Release / July 1, 2025
NS Pharma Announces Strategic Alliance with Boston Children’s Hospital to Develop New Therapies for Rare Diseases
Press Release / May 14, 2025
FDA Accepts Biologics License Application for Mucopolysaccharidosis II Treatment
Join us in Philadelphia this September for the FREE #CureDuchenne Workshop! Where families, caregivers and experts unite for learning, support, and connection.
This week, our brand ambassador Jordan picked his very first habaneros of the season which were perfect for making his famous JJ’s Firehouse Jam!🌶️🔥
His dedication reminds us how the right tools and a little creativity can make hobbies not just possible, but truly thriving. https://x.com/NSPharmaInc/status/1966167149107622229/photo/1
We’re excited to share that the FDA has granted Fast Track designation to NS-229 for Eosinophilic Granulomatosis with Polyangiitis (#EGPA), a rare autoimmune disease!
Read the full announcement: https://ow.ly/h95w50WTUFl
We're honored to be a sponsor of #WorldDuchenneAwarenessDay this weekend, brought to life by the @JettFoundation. Here's to making this year's louder than ever!